Development of an academic disease registry for spinal muscular atrophy
Published 7 January 2020 We report the development of a new disease registry on SMA as the result of a collaboration among three national networks in United States, Italy, and United Kingdom in partnership with a biotechnology company and with the support of advocacy groups. New publication in Neuromuscular Disorders
https://www.lupop.lu.se/article/development-academic-disease-registry-spinal-muscular-atrophy - 2025-02-28